Many women chalk up bloating or stomach changes to menopause — but experts warn these subtle signs are exactly why ovarian cancer is so often diagnosed late. If the risk climbs sharply after 45, how ...

Neuroinflammation, characterized by the activity of glial cells and the secretion of inflammatory cytokines, is a common pathological feature observed ...

Beam is advancing BEAM-304 using an approach in which multiple mutation-specific base editors are developed within a single clinical program.

Juan Uribe's 15-year-old son Max needs a perfect stem cell donor match. His story went viral on social media, but the search ...

New Program Designed as Platform-based Approach for Direct Correction of Mutations Causing PKU; Investigational New Drug (IND) Filing for ...

A new study has shed light on why patients with certain rare immune disorders develop severe, food-triggered allergic reactions while others with similar diagnoses do not. The findings, published in ...

Today, the FDA issued draft guidance outlining a new regulatory pathway intended to help sponsors gain approval for highly ...

For generations, the word "cancer" has been synonymous with a sense of inevitability; a roll of the genetic dice that few can escape. We often view it as a looming shadow that strikes without warning ...

FDA draft guidance could speed approval of individualized genome editing and RNA therapies for rare diseases. Read more here.

Engineers at the University of Pennsylvania and Rice University have refined a technology for editing individual genetic ...

TSRA-196 is designed to precisely correct the genetic mutation underlying AATD, with the goal of restoring production of functional alpha-1 antitrypsin (AAT) protein through a one-time, durable ...

The first gene therapies approved to treat sickle cell disease in December 2023 are struggling on the market. But there are ...