After a baby became the world's first CRISPR gene editing therapy patient, CHOP wants to expand treatment to others

One year after receiving CRISPR gene editing therapy at CHOP, a Delaware County baby is thriving, and doctors want to expand ...

Gene editing takes centre stage in FDA’s new rare disease approval pathway

"Gene editing takes centre stage in FDA’s new rare disease approval pathway" was originally created and published by ...

Engineers sharpen gene-editing tools to target cystic fibrosis

Engineers at the University of Pennsylvania and Rice University have refined a technology for editing individual genetic ...
BioSpace

FDA’s Bespoke Pathway To Focus on Gene Editing and RNA-Based Treatments for Rare Diseases

The framework, first introduced by FDA Commissioner Marty Makary and Center for Biologics Evaluation and Research head Vinay ...

Gene editing treatments could get easier FDA approval under new plan

FDA Commissioner Marty Makary says the agency wants to remove barriers for patients suffering from rare genetic conditions.

New targeted base-editing tool corrects genetic brain disorder in mice

Researchers have found that a new base-editing gene therapy can help treat a rare neurodevelopmental disorder called Snijders Blok–Campeau syndrome caused by mutations in the CHD3 gene. A specialized ...
Frontiers

Gene editing in vaccine development against vectors and vector-borne diseases (VBDs)

Vector-borne diseases (VBDs) represent a critical challenge in infectious disease control due to their complex transmission dynamics, diverse vector ...

Stronger scents and healthier crops: Unlocking plants' hidden potential through precision gene editing

Scientists have long sought to understand why some plants are fragrant powerhouses while others remain subtle. Now, a ...
Science Unbound on MSN

How gene editing could change humanity forever

Humans have been shaping life for thousands of years through farming, breeding, and selective cultivation. But with modern tools like CRISPR, we can now directly edit DNA itself—rewriting the very ...
WUSF Public Media

Studies test whether gene-editing can fix high cholesterol. For now, take your medicine

Gene-editing approaches being developed by two companies show hints that switching off certain genes could dramatically ...
Indian Defence Review on MSN

How CRISPR Could Turn the Tide in the Battle Against Antibiotic-Resistant Superbugs

A team of scientists has developed a cutting-edge CRISPR system that can not only combat antibiotic resistance but actively reverse it. This breakthrough could change the course of modern medicine, ...
BMJ Case Reports

Monoallelic PARN mutation presenting as pancytopenia, hepatic fibrosis and idiopathic pulmonary fibrosis

A woman in her late 20s presented with a 5-year history of progressive fatigue and generalised weakness. Examination revealed signs of premature ageing, anaemia, neuropathy and hepatosplenomegaly.