As Uganda rolls out mandatory nationwide screening of newborns for sickle cell disease this month, a gene therapy celebrated in the United States and Europe remains financially out of reach for most ...

Fulcrum Therapeutics, Inc. ( FULC) Q4 2025 Earnings Call February 24, 2026 8:00 AM EST Good morning, and welcome to the Fulcrum Therapeutics conference call to discuss 12-week data from the ...

The study, named IDEAL ( IaDademstat treatment for EssentiAL thrombocythemia ), is a multicenter, single-arm Phase II study to be conducted in Spain in adult patients with ET who are ...

Today, Kwincy Lassiter is a 25-year-old student enjoying a second chance at life. However, the first 16 years of his sickle cell journey looked much different.

Sickle cell anemia (HbSS) is the homozygous dominant variant and the most common and severe form of the disease. Whereas patients who only inherited one gene encoding for abnormal HbS and a different ...

Recent therapies like hydroxyurea (Droxia, Bristol-Myers Squibb), the first FDA-approved drug for SCD in 1994, increase fetal hemoglobin (HbF), which, through unknown pathways, improves SCD symptoms ...

New Bills coach Brady fills defensive coordinator job by hiring Leonhard ORCHARD PARK, N.Y. (AP) — The Buffalo Bills hired Jim Leonhard as their defensive coordinator under new head coach Joe ...

ROCHESTER, N.Y. — The School Without Walls will hold its fourth annual blood drive on Wednesday, which also aims to raise awareness for sickle cell disease. The student-led event started after a ...

A Black female doctor when that was rare, she developed a diagnostic test for the disease that is still a standard tool, as well as treatment guidelines. By Sam Roberts Dr. Angella D. Ferguson, a ...

Serenity Cole enjoyed Christmas last month relaxing with her family near her St. Louis home, making crafts and visiting friends. It was a contrast to how Cole, 18, spent part of the 2024 holiday ...

The Scottish Medicines Consortium (SMC) has accepted exagamglogene autotemcel (Casgevy, Vertex Pharmaceuticals) for use within NHS Scotland to treat sickle cell disease (SCD) in patients aged 12 years ...

INDIANAPOLIS (WISH) — For the first time, scientists say new therapies have the power to cure sickle cell disease. The disease is a devastating, inherited blood disorder that affects an estimated ...