One year after receiving CRISPR gene editing therapy at CHOP, a Delaware County baby is thriving, and doctors want to expand ...

Scientists have long sought to understand why some plants are fragrant powerhouses while others remain subtle. Now, a ...

To be the first person in the world cured of chronic granulomatous disease, a rare genetic condition, feels a little surreal ...

"Gene editing takes centre stage in FDA’s new rare disease approval pathway" was originally created and published by ...

Scientists achieved the smell by editing genes in tomatoes responsible for their aroma to make them smell similar to popcorn.

Engineers at the University of Pennsylvania and Rice University have refined a technology for editing individual genetic ...

After dumping its sole remaining gene therapy asset last year, Pfizer has decided to exercise its option for global rights to Beam Therapeutics’ liver-targeted gene editing candidate.

The framework, first introduced by FDA Commissioner Marty Makary and Center for Biologics Evaluation and Research head Vinay ...

CNBC's Becky Quick reports on the progress of KJ Muldoon, the first patient to receive a personalized CRISPR-based gene ...

Researchers have found that a new base-editing gene therapy can help treat a rare neurodevelopmental disorder called Snijders Blok–Campeau syndrome caused by mutations in the CHD3 gene. A specialized ...

Scientists generate world’s first ’extraordinary aromatic tomato plants’ by simultaneously altering two key genes ...

The first gene therapies approved to treat sickle cell disease in December 2023 are struggling on the market. But there are ...